Incremental Cost Per Quality-adjusted Life Year Gained? The Need for Alternative Methods to Evaluate Medical Interventions for Ultra-rare Disorders

Incremental Cost Per Quality-adjusted Life Year Gained? The Need for Alternative Methods to Evaluate Medical Interventions for Ultra-rare Disorders

2013 Value in health

Schlander, M. | Garattini, S. | Kolominsky-Rabas, P. | Nord, E. | Persson, U. | Postma, M. | Richardson, J. | Simoens, S. | Sola Morales, O. | Tolley, K. | Toumi, M. | Volume: 16, Issue: 7, Pages: A324, methods, Medicine, standards, Prevalence, economic evaluation, model,

To critically appraise the problems posed by the systematic valuation of interventions for ultra-rare disorders using conventional health economic analysis methods.